At Taysha Gene Therapies, we believe that with a steadfast focus on the targeted execution of our gene therapy programs, we can dramatically improve the lives of patients living with diseases of the central nervous system (CNS) caused by the mutation of a single gene, known as a monogenic disease.
And we believe that world is within our reach.
The Meaning of Taysha
Taysha is a word in the Caddo Native American language meaning “ally” or “friend,” and when translated, also means “Texas.”
We are committed to being an ally to the rare disease community and value the partnership of the patients and families we serve.
Our vision is bold. We’ve assembled the right pieces to help make it a reality.
A Disciplined Approach to Our Gene Therapy Programs
To achieve our goals of developing gene therapies that transform the lives of patients living with CNS diseases, we are tenaciously focused on our most promising therapeutic candidates. Our focus ensures that we are maximizing the potential to successfully deliver treatments to patients living with devastating diseases.
A Relentless Focus on Rett Syndrome
Our gene therapy candidate for Rett syndrome, TSHA-102, is designed to help address the technical challenges presented by one of the most common genetic causes of severe intellectual disability in females.
Experts in Gene Therapy and Putting Patients First
Our team is comprised of experts who led the development and commercialization of the first U.S. Food and Drug Administration (FDA) approved gene therapy to treat a monogenic disease of the CNS. We aim to build upon this proven track record and positively impact the lives of more patients and families impacted by CNS diseases.
Recent News
The latest from Taysha Gene Therapies
