Bringing New Cures to Life

At Taysha Gene Therapies, we believe in a world where monogenic CNS disease can be eradicated.

And we believe that world is within our reach.

What Does Taysha Mean?

Taysha is a word in the Caddo Native American language meaning “ally” or “friend,” and when translated, also means “Texas.” We are committed to being an ally to the rare disease community.

Our vision is bold, and we’ve assembled the right pieces to help make it a reality.

A new approach, based on a proven method.

Our strategy is to advance a pipeline of gene therapies that serve a population of patients who suffer from diseases with high unmet medical needs. Our proven approach bridges the gap between innovation and a potential cure.

Experts in gene therapy – and putting patients first.

We’ve reunited the top talent in gene therapy and together, we believe we can discover, develop, and commercialize novel gene therapies for both rare and large patient populations.

A pipeline built on 26 gene therapies.

We are advancing an extensive AAV gene therapy pipeline, with each medicine targeting the underlying biology of the specific indication. Our lead candidates include potential treatments for GM2 gangliosidosis, Rett syndrome and CLN1.